Annexon Accelerates Immunotherapy Development with Key Milestones for 2026
On January 12, 2026, Annexon, Inc. (Nasdaq: ANNX) announced significant advancements in its targeted immunotherapy platform, focused on treating neuroinflammatory diseases that affect nearly 10 million people globally. The company revealed its strategic priorities and crucial milestones aimed at bringing innovative therapies to market in 2026.
Major Developments in 2026
Annexon has outlined essential goals for this year, including:
- Potential approval for tanruprubart, targeting Guillain-Barré Syndrome (GBS).
- Anticipated release of pivotal Phase 3 topline data for vonaprument, which aims to protect vision in patients with dry AMD and geographic atrophy (GA).
- Proof-of-concept data expected for ANX1502, the first oral C1 inhibitor designed for autoimmune diseases.
- Strong financial health, projected to fund operations into late 2027 and beyond key milestones.
Tanruprubart: A Fast-Acting Solution for GBS
The Marketing Authorization Application (MAA) for tanruprubart has been filed with the European Medicines Agency. This therapy demonstrates a rapid impact on neuroinflammation, suggesting a faster recovery for patients when compared to standard treatments such as intravenous immunoglobulin (IVIg) or plasma exchange (PE).
Next milestones include a Biologics License Application (BLA) submission in 2026, supported by data from the ongoing FORWARD trial, which aims to broaden its application across various patient demographics.
Vonaprument: Protecting Vision in Patients with GA
Vonaprument is positioned to be the first targeted treatment preserving vision in patients with dry AMD and GA. The Phase 3 ARCHER II trial has been successfully completed, enrolling 659 patients ahead of schedule. This study focuses on preventing vision deterioration by measuring best corrected visual acuity (BCVA) over 15 months.
Annexon anticipates topline data from this trial in the second half of 2026, which is expected to contribute significantly to the understanding of vision protection mechanisms.
ANX1502: A Novel Approach to Autoimmune Disease
The upcoming proof-of-concept trial for ANX1502 is groundbreaking, as it represents the first oral treatment targeting C1 inhibition for autoimmune conditions. This current study focuses on pharmacokinetics and pharmacodynamics, which are vital for assessing dosage flexibility and efficacy in patients with cold agglutinin disease (CAD).
Updates regarding the trial findings are also expected throughout 2026, providing insights on its potential across neuromuscular autoimmune diseases.
About Annexon, Inc.
Annexon Biosciences (Nasdaq: ANNX) is committed to revolutionizing treatment for those suffering from serious neuroinflammatory diseases. The company's core focus is on understanding the role of C1q, a key mediator in neuroinflammation, as it seeks to develop therapies that provide meaningful benefits to patients.
For more information, visit annexonbio.com.
Forward-Looking Statements
This announcement contains forward-looking statements as defined under Section 27A of the Securities Act of 1933 and Section 21E of the Securities Exchange Act of 1934. These statements involve risks and uncertainties, including but not limited to anticipated regulatory timelines and the expected therapeutic benefits of its products.