Avidity Biosciences Honors Rare Disease Day® and Global Efforts to Support People and Families Impacted by Rare Neuromuscular Diseases
1. Avidity celebrates Rare Disease Day to raise awareness for rare diseases. 2. They support activities focusing on neuromuscular disorders like DMD and DM1. 3. Avidity's AOCs aim to improve RNA therapies for previously unreachable diseases. 4. Company emphasizes collaboration with advocacy groups and communities. 5. Leadership advocates the urgent need for approved treatments in rare diseases.